| Title | Targeting RNA structure in SMN2 reverses spinal muscular atrophy molecular phenotypes |
| Publication Type | Journal Article |
| Year of Publication | 2018 |
| Authors | Garcia-Lopez A, Tessaro F, Jonker HRA, Wacker A, Richter C, Comte A, Berntenis N, Schmucki R, Hatje K, Petermann O, Chiriano G, Perozzo R, Sciarra D, Konieczny P, Faustino I, Fournet G, Orozco M, Artero R, Metzger F, Ebeling M, Goeklian P, Joseph B, Schwalbe H, Scapozza L |
| Journal | Nat. Commun. |
